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RWD130 Healthcare Resource Utilization for Pediatric and Adolescent Duchenne Muscular Dystrophy Patients: Analysis of Real-World Data.
PCR141 The Impact of Duchenne Muscular Dystrophy on Caregiver Employment: A Survey in Europe, Japan, and the United States.
PIH4 NUMBER NEEDED TO TREAT (NNT) WITH FENFLURAMINE TO ACHIEVE A CLINICALLY MEANINGFUL REDUCTION IN CONVULSIVE SEIZURE FREQUENCY IN PATIENTS WITH DRAVET SYNDROME: HEALTH ECONOMIC IMPLICATIONS.