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Burosumab Therapy in Children with X-Linked Hypophosphatemia.
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.
Quintupling Inhaled Glucocorticoids to Prevent Childhood Asthma Exacerbations.
Exercise Type in Dieting Obese Older Adults.
Mechanisms, Pathophysiology, and Management of Obesity.
Antiretroviral Therapy for Perinatal HIV Prevention.
Caring for Children by Supporting Parents.
Multisystem Anomalies in Severe Combined Immunodeficiency with Mutant BCL11B.
Acetaminophen versus Ibuprofen in Young Children with Mild Persistent Asthma.
Treatment of Fabry's Disease with the Pharmacologic Chaperone Migalastat.