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Pediatric MDS: GATA screen the germline.
A booster shot to cure hemoglobinopathies.
The LSD1 inhibitor RN-1 induces fetal hemoglobin synthesis and reduces disease pathology in sickle cell mice.
Subclonal mutations in SETBP1 confer a poor prognosis in juvenile myelomonocytic leukemia.
Preclinical efficacy of MEK inhibition in Nras-mutant AML.
NRASG12V oncogene facilitates self-renewal in a murine model of acute myelogenous leukemia.
Bedside to bench in juvenile myelomonocytic leukemia: insights into leukemogenesis from a rare pediatric leukemia.
First do no harm: infectious deaths in pediatric ALL.
Hematopoietic stem cell dysfunction underlies the progressive lymphocytopenia in XLF/Cernunnos deficiency.
A(nother) RAF mutation in LCH.