Skip to main content
Donor lymphocyte infusion and methotrexate for immune recovery after T-cell depleted haploidentical transplantation.
Outcomes after 18 months of eliglustat therapy in treatment-naïve adults with Gaucher disease type 1: The phase 3 ENGAGE trial.
Lifespan care in SCD: Whom to transition, the patients or the health care system?
Transcranial doppler re-screening of subjects who participated in STOP and STOP II.
Fertility in transfusion-dependent thalassemia men: effects of iron burden on the reproductive axis.
Pain over time and its effects on life in thalassemia.
Efficacy and safety of deferasirox compared with deferoxamine in sickle cell disease: two-year results including pharmacokinetics and concomitant hydroxyurea.
Pregnancy outcomes in women with thalassemia in North America and the United Kingdom.
Safety and efficacy of velaglucerase alfa in Gaucher disease type 1 patients previously treated with imiglucerase.
Exercise performance in thalassemia major: correlation with cardiac iron burden.