Skip to main content
Application of a radiosensitivity flow assay in a patient with DNA ligase 4 deficiency.
Comparison of pediatric allogeneic transplant outcomes using myeloablative busulfan with cyclophosphamide or fludarabine.
The case for HLA-identical sibling hematopoietic stem cell transplantation in children with symptomatic sickle cell anemia.
Neurologic event-free survival demonstrates a benefit for SCID patients diagnosed by newborn screening.