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In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe's Disease.
Multicenter, Randomized Trial of a Bionic Pancreas in Type 1 Diabetes.
Trial of Erythropoietin for Hypoxic-Ischemic Encephalopathy in Newborns.
Maternal Vaccination and Risk of Hospitalization for Covid-19 among Infants.
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease.
Modeling Human Cardiac Chambers with Organoids.
Therapeutic Anticoagulation with Heparin in Noncritically Ill Patients with Covid-19.
Therapeutic Anticoagulation with Heparin in Critically Ill Patients with Covid-19.
Promoting Equity for Women in Medicine - Seizing a Disruptive Opportunity.
Induction of Fetal Hemoglobin by Gene Therapy.