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A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B.
CBFA2T3-GLIS2 model of pediatric acute megakaryoblastic leukemia identifies FOLR1 as a CAR T cell target.
Mass cytometry detects H3.3K27M-specific vaccine responses in diffuse midline glioma.
Clonal hematopoiesis in sickle cell disease.
To T or not to B: germline RUNX1 mutation preferences in pediatric ALL predisposition.
Mass cytometry detects H3.3K27M-specific vaccine responses in diffuse midline glioma.
Lack of Flvcr2 impairs brain angiogenesis without affecting the blood-brain barrier.
Bile acid metabolism is altered in multiple sclerosis and supplementation ameliorates neuroinflammation.
The Mir181ab1 cluster promotes KRAS-driven oncogenesis and progression in lung and pancreas.
Glucocorticoids paradoxically facilitate steroid resistance in T cell acute lymphoblastic leukemias and thymocytes.