In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial.

Marisa E. Schwab, Jennifer L. Cohen, Billie Lianoglou, Renata C. Gallagher, Juan M. Gonzalez-Velez, Teresa N. Sparks, Mary E. Norton, Michael H. Gelb, Tim Wood, Priya S. Kishnani, Paul R. Harmatz, Tippi C. MacKenzie