Impact of elosulfase alfa in patients with Morquio syndrome type A who have limited ambulation: An open-label, phase 2 study.

Paul R. Harmatz, Andrea Jester, Eugen Mengel, Marsha Treadwell, Barbara K. Burton, Kenneth I. Berger, Christian J. Hendriksz, Tarekegn Geberhiwot, Zlatko Sisic, Celeste Decker