AAV-SPL 2.0, a Modified Adeno-Associated Virus Gene Therapy Agent for the Treatment of Sphingosine Phosphate Lyase Insufficiency Syndrome.

International journal of molecular sciences

2023

https://researcherprofiles.org/profile/458953858

37958544

Khan R, Oskouian B, Lee JY, Hodgin JB, Yang Y, Tassew G, Saba JD