Betibeglogene Autotemcel (Beti-cel) Gene Addition Therapy Results in Durable Hemoglobin A (HbA) Production with up to 10 Years of Follow-up in Participants with Transfusion-Dependent ß-Thalassemia.

Timothy S. Olson, Alexis A. Thompson, Janet L. Kwiatkowski, Jennifer Schneiderman, Isabelle Thuret, Andreas E. Kulozik, Evangelia Yannaki, Marina Cavazzana, Suradej Hongeng, Martin G. Sauer, Adrian J. Thrasher, Ashutosh Lal, John E.J. Rasko, Hancheng Jiang, Ge Tao, Himal L. Thakar, Niki Witthuhn, Mark C. Walters, Franco Locatelli