Multi-Year Registry Study of Elapegademase Treatment in Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy.

Dorsey MJ, Butte MJ, Lieberman JA, Lehman H, Fausnight T, Keller MD, Fradette C, Hershfield MS, Pozos TC, Rozova A, Wall LA, Bednarski JJ, Tarrant TK, Chong HJ, Geng B, Temin NT, Laubach SS, Lin L, Mousallem T, Walter JE