Cipaglucosidase alfa and miglustat for treatment of late-onset Pompe disease (LOPD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG).
2025
https://researcherprofiles.org/profile/679821926
40893835
Baker EK, Derry A, Cohen JL, Chang IJ, ACMG Therapeutics Committee5*
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