Cell-Specific Evaluation of AAV9-Mediated SGPL1 Gene Delivery in a Sgpl1-/- Mouse Model with Nephrotic Syndrome.

Kraisoon Lomjansook, Gijs AC Franken, Katharina Lemberg, Ken Saida, Daniel Marchuk, Elena Zion, Chiranth M Prakash, Korbinian M. Riedhammer, Becca Nelson, Florian Buerger, Julie D. Saba, Friedhelm Hildebrandt