An Intravenous Brain-Penetrant Enzyme Therapy for Mucopolysaccharidosis II.

2026
https://researcherprofiles.org/profile/755915832
41467650
Muenzer J, Burton BK, Harmatz P, Rajan DS, Jones SA, van den Hout JMP, Mitchell JJ, Bhalla A, Engmann NJ, Zubizarreta I, Dong W, Model F, Watts RJ, Troyer MD, Chin PS, Ho C