Clinical characteristics and real-world outcomes in patients with mucopolysaccharidosis II over 18 years: final report of the Hunter Outcome Survey.

Muenzer J, Botha J, Amartino H, Giugliani R, Harmatz P, Kampmann C, Link B, Lin SP, Molter D, Raiman J, Scarpa M, Tylki-Szymanska A, Jain S, Whiteman DAH, Burton BK