Eculizumab for Pediatric Hematopoietic Cell Transplant Associated Thrombotic Microangiopathy: Real World Response Rates, Predictors of Poor Response, and an Optimal Timepoint for Treatment Response Assessment.

Schoettler ML, Cheng G, Higham CS, Dvorak CC, Rush C, Rangarajan HG, Al-Nazer M, Polishchuk V, Chaudhury S, Lehmann L, Duncan C, Nishitani M, Manougian H, Rotz S, Ofori J, Frost E, Orbodo J, Spencer K, Kenney E, Chonat S, Chewning J, Moore C, Westbrook A, Williams KM