Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

Jia K, Soupene E, Sinha R, Lesch BJ, Pendergast MA, Choi R, Zhang X, Foppiani EM, Kostamo Z, Chu SN, Sharma D, Yu X, Cordero M, Walters MC, MacKenzie TC, Sheehan VA, Cromer MK