Precision Medicine in Pediatric Autoimmunity: Leniolisib Treatment of Childhood-Onset Lupus Nephritis Due to Activated Phosphoinositide 3-Kinase δ Syndrome.
Lim JP, Ahmadian M, Du H, Rickert C, Ghosh T, Xing F, Minic A, Johnson SA, Weinman JP, Willard N, Lin C, Cooper JC, Hanna M, Knight V, Ghosh D, Jordan KR, Hsieh EWY