Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome.

2016
https://researcherprofiles.org/profile/118043547
27380995
Hendriksz CJ, Parini R, AlSayed MD, Raiman J, Giugliani R, Solano Villarreal ML, Mitchell JJ, Burton BK, Guelbert N, Stewart F, Hughes DA, Berger KI, Slasor P, Matousek R, Jurecki E, Shaywitz AJ, Harmatz PR