Long-term enzyme replacement therapy: Findings from the mucopolysaccharidosis VI clinical surveillance program after 15 years follow-up.

Molecular genetics and metabolism
2025
https://researcherprofiles.org/profile/616353764
40381595
Burton BK, Harmatz PR, Horvathova V, Lail A, Lampe C, Parini R, Sharma R, Teles EL