A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B.

2023
https://researcherprofiles.org/profile/366102626
36413418
Muschol N, Koehn A, von Cossel K, Okur I, Ezgu F, Harmatz P, de Castro Lopez MJ, Couce ML, Lin SP, Batzios S, Cleary M, Solano M, Nestrasil I, Kaufman B, Shaywitz AJ, Maricich SM, Kuca B, Kovalchin J, Zanelli E